Proyecto FINDLa importancia de un diagnóstico precoz

  1. Cristobal Colon Mejeras
Revista:
Acta pediátrica española

ISSN: 0001-6640

Ano de publicación: 2015

Volume: 73

Número: 3

Páxinas: 56-59

Tipo: Artigo

Outras publicacións en: Acta pediátrica española

Resumo

The mucopolysaccharidoses (MPS) are a heterogeneous group of lysosomal diseases caused by the enzymatic deficiency of glycosaminoglycans (GAG) degradation. Due to recent treatment advances and the fact that early diagnosis and treatment implicate a better clinical outcome, we have started the FIND project. This project is a selective screening to detect possible MPS cases in children using urine and blood samples impregnated in analytical paper, easily obtained in the Pediatrician consultation and supplied in the FIND kit. We carry out the GAG determination on urine sample. Over those urine samples with an elevated GAG concentration; we can perform the enzymatic activity on the blood sample, in order to identify the possible enzyme defect.